Category: Rare Disease

Cholestatic liver diseases are a rare but significant group of conditions that impact both children and adults. Three such conditions—Primary

. An article by Jennifer Schranz, Senior Vice President and Global Head of Rare Diseases at Ipsen In storytelling, you

. An article by Philippe Ghyssels, Vice President Corporate and Global Public Affairs For individuals living with a rare disease, every

Every day, millions of people around the world face the immense challenges of living with a rare disease. For these

. An article by Josep Catlla, Executive Vice President, Chief Corporate Affairs Officer “Each year, Rare Disease Day is a

. Only 1 in 30,000 children are born with ALGS each year1,2 This January, we are standing with the Alagille

A few months after Eva Luna was born, her mother Francesca realised something wasn’t quite right. Within the span of

Sandra Silvestri, Executive Vice President & Chief Medical Officer at Ipsen, reflects on the theme for this year’s PBC Awareness

“We’re often asked, what is the PBC journey? And the challenge is that, well, the PBC journey doesn’t exist. There