Developing innovation for people living with rare diseases is uniquely challenging. It requires all the different pieces of the puzzle–
Category: Rare Disease
Innovating for people living with primary biliary cholangitis
At Ipsen we have been focused on developing new and innovative treatments for rare diseases for many years in endocrinology,
Bridging the innovation gap in rare diseases
At the latest edition of European Health Forum Gastein, Ipsen held an interactive session to raise awareness of the challenges
PBC Awareness Month: The power of patient voices
As anyone living with Primary Biliary Cholangitis (PBC) – a rare and progressive autoimmune liver disease1 – knows, the disease
Mapping valuable insights from the FOP patient community in the UK and Spain
FOP is an ultra-rare genetic disorder where extra bone formation takes place in soft tissues, including muscles, tendons and ligaments,
Putting yourself in the shoes of someone with an ultra-rare condition: the first FOP immersive experience
You can never truly understand what it’s like to live with an ultra-rare condition unless you’ve experienced it for yourself.
Understanding the Person Behind the Chart – Living with Primary Biliary Cholangitis
Primary biliary cholangitis (PBC) is a chronic autoimmune disease that affects liver function and can have debilitating symptoms for people
Learning the impacts of FOP from patients and their families – The Burden of Illness study
Fibrodysplasia ossificans progressiva (FOP) is an ultra-rare genetic disorder where extra bone formation takes place in soft tissues, including muscles,
Primary Biliary Cholangitis (PBC): Looking Beyond the Liver
“Symptom burden is the main issue for the patient.”– Professor Andreas Kremer, Hepatologist of the University of Zurich Hospital Primary
Advancing Primary Biliary Cholangitis (PBC) Management: Insights from Experts
“We are on the cusp of an absolute explosion in our approach to managing PBC.” – Professor Gideon Hirschfield, Hepatologist