Category: Rare Disease

Sandra Silvestri, Executive Vice President & Chief Medical Officer at Ipsen, reflects on the challenges women living with primary biliary

Progressive Familial Intrahepatic Cholestasis (PFIC) is a rare liver disease that can pose significant challenges, particularly in young children1, but

At seventy-one-years young, Gill, a devoted mother and grandmother from Nottinghamshire, loves spending time with her grandchildren and gardening. She

Sabrina is a lover of nature, mother and grandmother, whose outlook on life is to make every moment count. Sabrina

Every four years, Rare Disease Day lands on the ‘rarest’ day of the year, 29th February. Due to leap years,

Hearing a rare liver disease diagnosis can be one of the most emotionally turbulent moments in a person’s life.1 For

“The important thing with PBC is to take a holistic view of it, and think ‘What are the problems we

Jennifer Schranz (Ipsen’s Global Head of Rare Diseases) attended The Liver Meeting from November 10-14, sharing key insights from her

Developing innovation for people living with rare diseases is uniquely challenging. It requires all the different pieces of the puzzle–

At Ipsen we have been focused on developing new and innovative treatments for rare diseases for many years in endocrinology,