Rare Disease Archives

Breaking Barriers to Rare Disease Innovation: Reflections from the World EPA Congress

. An article by Philippe Ghyssels, Vice President Corporate and Global Public Affairs For individuals living with a rare disease, every

Every day, millions of people around the world face the immense challenges of living with a rare disease. For these

. An article by Josep Catlla, Executive Vice President, Chief Corporate Affairs Officer “Each year, Rare Disease Day is a

. Only 1 in 30,000 children are born with ALGS each year1,2 This January, we are standing with the Alagille

Biliary Atresia (BA) is a rare liver disease that usually appears in the first month of a baby’s life.1 In

A few months after Eva Luna was born, her mother Francesca realised something wasn’t quite right. Within the span of

Mature Female Friends Socializing In Backyard Together

Sandra Silvestri, Executive Vice President & Chief Medical Officer at Ipsen, reflects on the theme for this year’s PBC Awareness

“We’re often asked, what is the PBC journey? And the challenge is that, well, the PBC journey doesn’t exist. There

During the European Association for the Study of the Liver (EASL) congress, leading liver experts, Dr Mark Swain, Dr Emma

At the European Association for the Study of the Liver (EASL) congress, leading liver experts discuss the importance of proactive,